Adrenoleukodystrophy - 58 Studies Found
Recruiting |
: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells :
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Completed |
: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation :
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Recruiting |
: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis :
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Completed |
: Stem Cell Transplant for Inborn Errors of Metabolism :
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Recruiting |
: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis :
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Completed |
: Betaine and Peroxisome Biogenesis Disorders : Peroxisome Biogenesis Disorders : 2013-03-29 : Drug: Betaine Betaine will be given orally (mixed with foo |
Recruiting |
: A Pilot Study of Vitamin D in Boys With X-linked Adrenoleukodystrophy : X-linked Adrenoleukodystrophy : 2015-10-29 : Dietary Supplement: vitamin D3 Daily oral supplement provided by study investigators |
Completed |
: The Effect of Bezafibrate on the Level of Very Long Chain Fatty Acids (VLCFA) in X-linked Adrenoleukodystrophy (X-ALD) :
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Withdrawn |
: Safety and Pharmacodynamic Study of Sobetirome in X-Linked Adrenoleukodystrophy (X-ALD) :
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